PNH Registry: Published MANUSCRIPTS
| Full Title | Journal (Year) | Citation |
| Baseline characteristics and disease burden in patients in the International Paroxysmal Nocturnal Hemoglobinuria Registry | Haematologica (2014) | Schrezenmeier H, Muus P, Socié G, Szer J, Urbano-Ispizua A, Maciejewski JP, Brodsky RA, Bessler M, Kanakura Y, Rosse W, Khursigara G, Bedrosian C, Hillmen P. Baseline characteristics and disease burden in patients in the International Paroxysmal Nocturnal Hemoglobinuria Registry. Haematologica. 2014 May;99(5):922-9. |
| Eculizumab in Pregnant Patients with Paroxysmal Nocturnal Hemoglobinuria | New England Journal of Medicine (2015) | Kelly RJ, Höchsmann B, Szer J, Kulasekararaj A, de Guibert S, Röth A, Weitz IC, Armstrong E, Risitano AM, Patriquin CJ, Terriou L, Muus P, Hill A, Turner MP, Schrezenmeier H, Peffault de Latour R. Eculizumab in Pregnant Patients with Paroxysmal Nocturnal Hemoglobinuria. N Engl J Med. 2015 Sep 10;373(11):1032-9 |
| Changing prognosis in paroxysmal nocturnal haemoglobinuria disease subcategories: an analysis of the International PNH Registry | Internal Medicine Journal (2016) | Socié G, Schrezenmeier H, Muus P, Lisukov I, Röth A, Kulasekararaj A, Lee JW, Araten D, Hill A, Brodsky R, Urbano-Ispizua A, Szer J, Wilson A, Hillmen P; PNH Registry. Changing prognosis in paroxysmal nocturnal haemoglobinuria disease subcategories: an analysis of the International PNH Registry. Intern Med J. 2016 Sep;46(9):1044-53. |
| Characteristics of Taiwanese patients of PNH in the international PNH registry | Thrombosis Journal (2016) | Chou WC, Huang WH, Wang MC, Chang CS, Yeh SP, Chiou TJ, Chen YC, Lin TH, Shen MC. Characteristics of Taiwanese patients of PNH in the international PNH registry. Thromb J. 2016 Oct 4;14(Suppl 1):39. eCollection 2016. |
| Clinical benefit of eculizumab in patients with no transfusion history in the International Paroxysmal Nocturnal Haemoglobinuria Registry | Internal Medicine Journal (2017) | Almeida AM, Bedrosian C, Cole A, et al. Clinical benefit of eculizumab in patients with no transfusion history in the International Paroxysmal Nocturnal Haemoglobinuria Registry. Intern Med J. 2017;47(9):1026-1034. |
| Different clinical characteristics of paroxysmal nocturnal hemoglobinuria in pediatric and adult patients | Haematologica (2017) | Urbano-Ispizua Á, Muus P, Schrezenmeier H, Almeida AM, Wilson A, Ware RE. Different clinical characteristics of paroxysmal nocturnal hemoglobinuria in pediatric and adult patients. Haematologica. 2017 Mar;102(3):e76-e79. |
| Clinical course and disease burden in patients with paroxysmal nocturnal hemoglobinuria by hemolytic status | Blood Cells, Molecules & Diseases (2017) | Yenerel MN, Muus P, Wilson A, Szer J. Clinical course and disease burden in patients with paroxysmal nocturnal hemoglobinuria by hemolytic status. Blood Cells Mol Dis. 2017 Jun;65:29-34. |
| Clinical features and quality of life assessment in Japanese PNH patients enrolled in
the International PNH Registry
[Article in Japanese] |
Rinsho Ketsueki. [The Japanese Journal of Clinical Hematology] (2017) | Sakurai M, Okamoto S. Clinical features and quality of life assessment in Japanese PNH patients enrolled in the International PNH Registry. Rinsho Ketsueki. 2017;58(11):2261-2267. |
| The effectiveness of eculizumab in patients with paroxysmal nocturnal hemoglobinuria (PNH) in the international PNH registry who have high disease activity with or without history of aplastic anemia | American Journal of Hematology (2019) | Lee JW; Peffault de Latour R; Brodsky RA; Jang JH; Hill A; Röth A; Schrezenmeier H; Wilson A; Marantz JL; Maciejewski JP. The effectiveness of eculizumab in patients with paroxysmal nocturnal hemoglobinuria (PNH) in the international PNH registry who have high disease activity with or without history of aplastic anemia Am J Hematol. 2019 Jan;94(1):E37-E41. |
| Comparative study on baseline clinical characteristics of Asian versus non-Asian patients with paroxysmal nocturnal hemoglobinuria. | International Journal of Hematology (2019) | Sakurai M, Jang JH, Chou WC, Kim JS, Wilson A, Nishimura JI, Chiou TJ, Kanakura Y, Lee JW, Okamoto S. Comparative study on baseline clinical characteristics of Asian versus non-Asian patients with paroxysmal nocturnal hemoglobinuria. Int J Hematol. 2019 Oct;110(4):411-418. |
| Baseline clinical characteristics and disease burden in patients with paroxysmal nocturnal hemoglobinuria (PNH): Updated analysis from the International PNH Registry | Annals of Hematology (2020) | Schrezenmeier H, Röth A, Araten DJ, Kanakura Y, Larratt L, Shammo JM, Wilson A, Shayan G, Maciejewski JP. Baseline clinical characteristics and disease burden in patients with paroxysmal nocturnal hemoglobinuria (PNH): updated analysis from the international PNH Registry. Ann Hematol. 2020 Jul;99(7):1505-1514. |
| Benefits of eculizumab regardless of prior transfusions or bone marrow disease: results of the International Paroxysmal Nocturnal Hemoglobinuria Registry | European Journal of Haematology (2020) | Röth A, Araten DJ, Larratt L, Kulasekararaj AG, Maciejewski JP, Wilson A, Gustovic P, Kanakura Y. Beneficial effects of eculizumab regardless of prior transfusions or bone marrow disease: Results of the International Paroxysmal Nocturnal Hemoglobinuria Registry. Eur J Haematol. 2020;00:1-10. |
| Effect of eculizumab treatment in patients with paroxysmal nocturnal hemoglobinuria with or without high disease activity: Real-world findings from the International Paroxysmal Nocturnal Hemoglobinuria Registry | European Journal of Haematology (2022) | Höchsmann B, Sicre de Fontbrune F, Lee JW, Kulagin AD, Hillmen P, Wilson A, Marantz JL, Schrezenmeier H. Effect of eculizumab treatment in patients with paroxysmal nocturnal hemoglobinuria with or without high disease activity: Real-world findings from the International Paroxysmal Nocturnal Hemoglobinuria Registry. Eur J Haematol. 2022;1-8. |